Assay Catalog
Available and customizable assays, protocols, and study designs — built from first-principles expertise in gene editing and translational biology. All entries can be tailored to your specific program, cell type, and regulatory context.
ddPCR Editing Efficiency Assay
Quantification of CRISPR editing rates (insertions, deletions, substitutions) in cell and tissue samples using digital droplet PCR. Includes primer/probe design, linearity, precision, specificity, LoD/LoQ determination.
Genome-Wide CRISPR KO Screen
Full-service genome-scale loss-of-function screens in human cell lines or primary cells. Includes library selection, lentiviral transduction, selection, NGS library deconvolution, and MAGeCK statistical analysis.
Perturb-seq Study Design & Execution
Single-cell CRISPR perturbation profiling for AI/ML training datasets. Full-service from experimental design through sgRNA library construction, 10x Chromium run, QC, and structured data delivery in AI-compatible formats.
NGS Off-Target Detection Panel
Unbiased genome-wide detection of CRISPR off-target editing using GUIDE-seq, CIRCLE-seq, or targeted amplicon NGS. Includes bioinformatics pipeline, candidate site ranking, and regulatory-ready reporting.
CD34+ HSC Engineering Protocol
Optimized CRISPR RNP electroporation and culture conditions for primary human CD34+ hematopoietic stem and progenitor cells. Includes cryopreservation, viability QC, and editing efficiency verification by ddPCR.
CRISPRa/i Functional Screen
Transcriptional activation or repression screens for gene regulatory network mapping. Uses dCas9-VPR (activation) or dCas9-KRAB (repression) with custom sgRNA libraries. Readout by NGS or flow-based enrichment.
Base Editing Efficiency Assay
Precise quantification of adenine base editor (ABE) or cytosine base editor (CBE) outcomes at target loci. Detects on-target base conversion, bystander edits, and indel frequency using ddPCR or amplicon-based NGS.
Clinical Biomarker Assay Package
IND-enabling biomarker assay development, analytical qualification, and validation. Customized for your specific biomarker (genetic, protein, or cell-based) with GLP-aligned documentation suitable for regulatory submissions.
Cas13d RNA Knockdown Panel
Quantitative assessment of Cas13d-mediated RNA knockdown efficiency and specificity across multiple target transcripts. Detects on-target and collateral cleavage activity using RT-qPCR and transcriptome-wide RNA-seq readout.
Multiplexed Editing Verification Panel
Simultaneous verification of multiple gene edits in a single patient or research sample using multiplex ddPCR. Enables streamlined clinical sample testing with high throughput and sensitivity for complex editing strategies.
| Assay / Kit Name | Intended Application | Technology Platform | Status |
|---|---|---|---|
| ddPCR Editing Efficiency AssayQuantification of CRISPR editing rates by digital PCR | Editing QC, IND Biomarker | ddPCR / Bio-Rad | Available |
| Genome-Wide CRISPR KO ScreenFull-service pooled loss-of-function screen with analysis | Target Discovery, Validation | CRISPR / NGS | Available |
| Perturb-seq Study Design & ExecutionSingle-cell perturbation profiling for AI/ML | AI/ML Training Datasets | 10x Chromium + CRISPR | Available |
| NGS Off-Target Detection PanelUnbiased genome-wide off-target detection | Safety, IND Filing | GUIDE-seq / Illumina NGS | Available |
| CD34+ HSC Engineering ProtocolRNP electroporation and culture optimization for HSCs | Gene Therapy Development | Electroporation / ddPCR | Customizable |
| CRISPRa/i Functional ScreenTranscriptional activation or repression screens | Gene Regulation Mapping | CRISPRa/CRISPRi + NGS | Customizable |
| Base Editing Efficiency AssayABE/CBE outcome quantification at target loci | Base Editing QC, IND | ddPCR / Amplicon NGS | Customizable |
| Clinical Biomarker Assay PackageIND-enabling biomarker qualification and validation | Clinical Trials, IND Filing | ddPCR / NGS / ELISA | Customizable |
| Cas13d RNA Knockdown PanelCas13d-mediated knockdown efficiency and specificity | RNA Targeting Therapeutics | RT-qPCR / RNA-seq | In Development |
| Multiplexed Editing Verification PanelSimultaneous multi-gene edit verification | Clinical Monitoring | Multiplex ddPCR | In Development |
Custom Assay Development
Every assay listed here can be adapted to your cell type, therapeutic modality, regulatory context, and timeline. If you have a biomarker or readout that isn't listed, we design custom solutions from first principles.
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